
KRYS+82.20%14.3%

NTLA-39.75%14.3%

QURE-57.18%14.3%

RARE-51.93%14.3%

SLNO0.00%14.3%

SRPT-18.88%14.3%

SRRK+32.81%14.3%
As of Oct 2, 2026, 9:55 PM ET
Rare Diseases '25: Gene Therapy & Genetic Med Constituents
Intellia Therapeutics, Inc.NTLA | 14.3% | 1.16% | -2.96% | -3.49% | 1.61% | 36.99% | -10.63% | 68.70% | -39.75% | -30.54% | -90.85% | $1.71B |
Krystal Biotech, Inc.KRYS | 14.3% | -0.93% | -5.65% | -10.34% | 1.76% | 34.27% | 20.10% | 82.90% | 82.20% | 83.19% | 498.03% | $9.50B |
Sarepta Therapeutics, Inc.SRPT | 14.3% | -0.40% | -12.88% | -21.89% | 3.19% | -15.75% | 8.17% | -70.98% | -18.88% | -85.26% | -81.78% | $1.85B |
Scholar Rock Holding CorporationSRRK | 14.3% | 1.41% | -8.70% | -16.69% | 1.25% | 6.10% | 5.57% | 43.62% | 32.81% | 562.09% | 46.28% | $5.61B |
Soleno Therapeutics, Inc.SLNO | 14.3% | 0.00% | 0.00% | 0.00% | 0.00% | 0.00% | 0.00% | 0.00% | 0.00% | 0.00% | 0.00% | $1.06B |
Ultragenyx Pharmaceutical Inc.RARE | 14.3% | 3.19% | -4.87% | -44.01% | 0.71% | -35.41% | -36.49% | -58.00% | -51.93% | -71.64% | -82.67% | $1.50B |
uniQure N.V.QURE | 14.3% | 0.39% | -48.47% | -49.52% | -0.15% | -2.49% | 49.30% | 119.73% | -57.18% | 414.47% | -26.76% | $1.63B |
| Theme return | — | 0.69% | -11.93% | -20.58% | 0.81% | 13.36% | 11.87% | 28.18% | 2.27% | 18.59% | -12.55% | — |
| Average | 14.3% | 0.69% | -11.93% | -20.85% | 1.20% | 3.39% | 5.15% | 26.57% | -7.53% | 124.62% | 37.47% | $3.26B |
| Median | 14.3% | 0.39% | -5.65% | -16.69% | 1.25% | 0.00% | 5.57% | 43.62% | -18.88% | 0.00% | -26.76% | $1.71B |
| Std Dev | 0.0% | 1.27% | 15.39% | 17.82% | 1.07% | 23.93% | 24.47% | 66.86% | 46.81% | 238.83% | 193.78% | $2.91B |
| Min | 14.3% | -0.93% | -48.47% | -49.52% | -0.15% | -35.41% | -36.49% | -70.98% | -57.18% | -85.26% | -90.85% | $1.06B |
| Max | 14.3% | 3.19% | 0.00% | 0.00% | 3.19% | 36.99% | 49.30% | 119.73% | 82.20% | 562.09% | 498.03% | $9.50B |
| % Positive Tickers | 57.14% | 0.00% | 0.00% | 71.43% | 42.86% | 57.14% | 57.14% | 28.57% | 42.86% | 28.57% |